Varsha JainLaura HansonSanthosh SethuramanujamTracy MichaelsJerram GawleyRonald G. GreggIan PyleChi ZhangRobert G. SmithDavid BersonMaureen A. McCallGautam B. Awatramani
central nervous systemneurophysiologyneuroscienceultra-slow glycinergic synapsescell biologycellular neurobiologygain controlsystems neurosciencephysiology
Allele-Selective Reduction of P23H-Mutant Rhodopsin With Stereopure Oligonucleotides Rescues Phenotype Associated With Retinitis Pigmentosa in Preclinical Models. Investigative Ophthalmology & Visual Science (2021)
Michael ByrneVinod VathipadickalLankai GuoYuan YinHailin YangRichard LoobyLauren NorwoodJames W Fransenarchana jalligampalaJennifer NoelChandra VargeeseMaureen A McCall
Ying Kai ChanSean K. WangColin J. ChuDavid A. CoplandAlexander J. LetiziaHelena Costa VerderaJessica J. ChiangMeher SethiMay K. WangWilliam J. NeidermyerYingleong ChanElaine T. LimAmanda R. GravelineMelinda SanchezRyan F. BoydThomas S. VihtelicRolando Gian Carlo O. InciongJared M. SlainPriscilla J. AlphonseYunlu XueLindsey R. Robinson-McCarthyJenny M. TamMaha H. JabbarBhubanananda SahuJanelle F. AdeniranManish MuhuriPhillip W. L. TaiJun XieTyler B. KrauseAndyna VernetMatthew PezoneRu XiaoTina LiuWei WangHenry J. KaplanGuangping GaoAndrew D. DickFederico MingozziMaureen A. McCallConstance L. CepkoGeorge M. Church
Rho 1-2 Meganuclease, an Allele-Specific Gene-Editing Therapy, Rejuvenates Rod Photoreceptor Structure and Function in a Pig Model of Autosomal Dominant Retinitis Pigmentosa (Adrp).. Investigative Ophthalmology & Visual Science (2021)
archana jalligampalaJennifer NoelJames W FransenWei WangMaha JabbarNazarul HasanGobinda PangeniBhubanananda SahuWhitney LewisJeff SmithVictor BartsevichKristi VilesDerek JantzMaureen A McCall
Spvn06, a Novel Mutation-Independent Aav-Based Gene Therapy, Protects Cone Degeneration in a Pig Model of Retinitis Pigmentosa. Investigative Ophthalmology & Visual Science (2021)
Jennifer Noelarchana jalligampalaMyriam MarussigPierre-Axel VinotMelanie MarieMelanie ButlerFlorence LorgetStephane BoisselThierry D LeveillardJose Alain SahelMaureen A McCall
Allele-Specific Homing Endonuclease (He) Gene Editing Induces Rod Function in a P23H Transgenic Swine Model of Retinitis Pigmentosa. Investigative Ophthalmology & Visual Science (2020)
James W Fransenarchana jalligampalaJennifer NoelWei WangJeff SmithVictor BartsevichKristi VilesMaureen A McCall
An Allele-Independent Gene Therapy Strategy Induces Rod Function in a Transgenic Swine Model of Autosomal Dominant Retinitis Pigmentosa. Investigative Ophthalmology & Visual Science (2020)
archana jalligampalaJames FransenJennifer NoelGobinda PangeniMaha Haleem JabbarWilliam W HauswirthAlfred S LewinMaureen A McCall